Family Screening in Relatives at Risk for Plakophilin-2–Associated Arrhythmogenic Right Ventricular Cardiomyopathy

Jan 1, 2025·
MD Steven A. Muller
,
J. Hopkins
,
Arvc Program
,
MD Babken Asatryan
,
PhD Alessio Gasperetti
,
PhD Maarten
,
MD J. Cramer
,
P. Amin
,
Peter Loh
,
PhD Richard T. Carrick
,
PhD Moniek G. P. J. Cox
,
Priya Md
,
PhD Marish
,
MD PhD I. F. J. Oerlemans
,
Mgc RN Crystal Tichnell
,
MD PhD Sing-Chien Yap
,
MS Cgc Brittney Murray
,
MD Stefan L. Zimmerman
,
MD PhD Hugh Peter Van Tintelen
,
M. Calkins
,
MD Te Riele
,
PhD Cynthia A. James
· 0 min read
Abstract
BACKGROUND: Penetrance and risk of ventricular arrhythmias (VAs) in arrhythmogenic right ventricular cardiomyopathy (ARVC) are increasingly recognized as being genotype specific. Therefore, genotype-informed family screening protocols may lead to safer and more personalized recommendations than the current one-size-fits-all screening recommendations. We aimed to develop a safe, evidence-based plakophilin-2 (PKP2)–specific longitudinal screening algorithm. METHODS: We included 295 relatives (41% male; age 30.9 years [18.0–47.7 years]) with a pathogenic or likely pathogenic PKP2 variant from 145…
Type
Publication
Circulation